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Medications for Gaucher Disease

Drugs associated with Gaucher Disease

The following drugs and medications are in some way related to, or used in the treatment of this condition.

What is Gaucher Disease: An inherited deficiency of an enzyme (-glucosidase) which results in the buildup of a toxic substance (glucosylceramide) in different parts of the body, such as the spleen, liver, and bones.

Drug name Rx / OTC Pregnancy CSA Alcohol Reviews Rating Popularity
VPRIV Rx B N Add review Add

Generic name: velaglucerase alfa systemic

Drug class: lysosomal enzymes

For consumers: dosage, side effects

For professionals: AHFS DI Monograph, Prescribing Information

 
Cerezyme Rx C N 1 review
9.0

Generic name: imiglucerase systemic

Drug class: lysosomal enzymes

For consumers: dosage, interactions, side effects

For professionals: AHFS DI Monograph, Prescribing Information

 
Zavesca Rx C N Add review Add

Generic name: miglustat systemic

Drug class: miscellaneous metabolic agents

For consumers: dosage, interactions, side effects

For professionals: AHFS DI Monograph, Prescribing Information

 
Elelyso Rx B N Add review Add

Generic name: taliglucerase alfa systemic

Drug class: lysosomal enzymes

For consumers: dosage, side effects

For professionals: AHFS DI Monograph

 
Cerdelga Rx C N Add review Add

Generic name: eliglustat systemic

Drug class: miscellaneous metabolic agents

For consumers: dosage, interactions, side effects

For professionals: Prescribing Information

 
imiglucerase Rx C N 1 review
9.0

Generic name: imiglucerase systemic

Brand name:  Cerezyme

Drug class: lysosomal enzymes

For consumers: dosage, interactions, side effects

For professionals: A-Z Drug Facts, AHFS DI Monograph

 
taliglucerase alfa Rx B N Add review Add

Generic name: taliglucerase alfa systemic

Brand name:  Elelyso

Drug class: lysosomal enzymes

For consumers: dosage, side effects

For professionals: A-Z Drug Facts, AHFS DI Monograph, Prescribing Information

 
velaglucerase alfa Rx B N Add review Add

Generic name: velaglucerase alfa systemic

Brand name:  VPRIV

Drug class: lysosomal enzymes

For consumers: dosage, side effects

For professionals: A-Z Drug Facts, AHFS DI Monograph

 
miglustat Rx C N Add review Add

Generic name: miglustat systemic

Brand name:  Zavesca

Drug class: miscellaneous metabolic agents

For consumers: dosage, interactions, side effects

For professionals: A-Z Drug Facts, AHFS DI Monograph

 
eliglustat Rx C N Add review Add

Generic name: eliglustat systemic

Brand name:  Cerdelga

Drug class: miscellaneous metabolic agents

For consumers: dosage, interactions, side effects

For professionals: A-Z Drug Facts

 
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Topics under Gaucher Disease

Learn more about Gaucher Disease

Legend

Off Label This medication may not be approved by the FDA for the treatment of this condition.
Prescription Only / Over the Counter
Rx Prescription Only
OTC Over the Counter
Rx/OTC Prescription or Over the Counter
Pregnancy
A Adequate and well-controlled studies have failed to demonstrate a risk to the fetus in the first trimester of pregnancy (and there is no evidence of risk in later trimesters).
B Animal reproduction studies have failed to demonstrate a risk to the fetus and there are no adequate and well-controlled studies in pregnant women.
C Animal reproduction studies have shown an adverse effect on the fetus and there are no adequate and well-controlled studies in humans, but potential benefits may warrant use of the drug in pregnant women despite potential risks.
D There is positive evidence of human fetal risk based on adverse reaction data from investigational or marketing experience or studies in humans, but potential benefits may warrant use of the drug in pregnant women despite potential risks.
X Studies in animals or humans have demonstrated fetal abnormalities and/or there is positive evidence of human fetal risk based on adverse reaction data from investigational or marketing experience, and the risks involved in use of the drug in pregnant women clearly outweigh potential benefits.
N FDA has not classified the drug.
Controlled Substances Act Schedule
N The drug is not subject to the Controlled Substances Act.
1 The drug has a high potential for abuse. The drug has no currently accepted medical use in treatment in the United States. There is a lack of accepted safety for use of the drug under medical supervision.
2 The drug has a high potential for abuse. The drug has a currently accepted medical use in treatment in the United States or a currently accepted medical use with severe restrictions. Abuse of the drug may lead to severe psychological or physical dependence.
3 The drug has a potential for abuse less than the drugs in schedules 1 and 2. The drug has a currently accepted medical use in treatment in the United States. Abuse of the drug may lead to moderate or low physical dependence or high psychological dependence.
4 The drug has a low potential for abuse relative to the drugs in schedule 3. The drug has a currently accepted medical use in treatment in the United States. Abuse of the drug may lead to limited physical dependence or psychological dependence relative to the drugs in schedule 3.
5 The drug has a low potential for abuse relative to the drugs in schedule 4. The drug has a currently accepted medical use in treatment in the United States. Abuse of the drug may lead to limited physical dependence or psychological dependence relative to the drugs in schedule 4.
Alcohol
X Interacts with Alcohol.

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