Medications for Metabolic Disorders
Topics under Metabolic Disorders
- Acid Sphingomyelinase Deficiency (2 drugs)
- Acidosis (1 drug)
- Adenosine Deaminase Deficiency (2 drugs)
- Alkalosis (1 drug)
- Alpha-Mannosidosis (2 drugs)
- Cystinuria (9 drugs)
- Fabry Disease (6 drugs)
- Gaucher Disease (11 drugs in 2 topics)
- Hereditary Orotic Aciduria (2 drugs)
- Hereditary Tyrosinemia Type 1 (3 drugs)
- Homocystinuria (2 drugs)
- Hutchinson-Gilford Syndrome (2 drugs)
- Iron Overload (7 drugs in 2 topics)
- Long-Chain Fatty Acid Oxidation Disorders (2 drugs)
- Lysosomal Acid Lipase Deficiency (2 drugs)
- Mucopolysaccharidosis Type I (2 drugs)
- Mucopolysaccharidosis Type II (2 drugs)
- Mucopolysaccharidosis Type IV (2 drugs)
- Mucopolysaccharidosis Type VI (2 drugs)
- Mucopolysaccharidosis Type VII (2 drugs)
- Nephropathic Cystinosis (3 drugs)
- Niemann-Pick Disease (5 drugs)
- Phenylketonuria (5 drugs)
- Pompe Disease (8 drugs)
- Porphyria (7 drugs in 2 topics)
- Primary Hyperoxaluria (4 drugs)
- Sucrase-Isomaltase Deficiency (2 drugs)
- Urea Cycle Disorders (6 drugs)
- Weight Loss (Obesity/Overweight) (38 drugs in 2 topics)
Further information
Always consult your healthcare provider to ensure the information displayed on this page applies to your personal circumstances.