Skip to main content

Is there a specific age range for which Exondys 51 will work?

Medically reviewed by Carmen Pope, BPharm. Last updated on Feb 23, 2023.

Official answer


There is currently no specific age range specified for using Exondys 51, but a two-part Phase 3 study scheduled to run until 2026 has recruited boys and young men aged 4 though 21 who meet the study criteria. Previous studies have only investigated boys up to age 19 years. Symptoms of Duchenne muscular dystrophy (DMD) usually appear between 3 and 5 years of age and the condition primarily affects boys at a rate of about 1 in every 3,600 male infants born. If you have an older child, the best thing you can do is talk to your doctor about Exondys 51 treatment.

  • Madesen A. Top 5 FAQs: Eteplirsen (Exondys 51) for DMD Treatment Sept 2016. MDA News.
  • Exondys 51. Sarepta

Read next

Related medical questions

Drug information

Related support groups