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Duchenne Muscular Dystrophy Support Group

Summary

Our support group for Duchenne Muscular Dystrophy has 11 questions and 4 members. Updated 8 Jul 2024.

Featured questions

How is Vyondys 53 administered?

How does Vyondys 53 work?

How is Exondys 51 administered?

Is Exondys 51 a type of gene therapy?

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Further information

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Latest news

Drug Safety Communication: FDA Investigating Deaths Due to Acute Liver Failure in Non-Ambulatory Duchenne Muscular Dystrophy Patients Following Elevidys

FDA Safety Communication – June 24, 2025 – Since approval, the Food and Drug Administration (FDA) has received two…

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