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Muscular Dystrophy News

Related terms: Myotonic Muscular Dystrophy, Myotonic Dystrophy, Dystrophia Myotonica, Steinert's Disease, Becker Muscular Dystrophy, MD, Emery-Dreifuss Muscular Dystrophy, Facioscapulohumeral Muscular Dystrophy

FDA Approves Vyondys 53 (golodirsen) Injection for the Treatment of Duchenne Muscular Dystrophy (DMD) in Patients Amenable to Skipping Exon 53

CAMBRIDGE, Mass., Dec. 12, 2019 (GLOBE NEWSWIRE) – Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, today announced that the U.S. Food and Drug...

FDA Approves Emflaza (deflazacort) to treat Duchenne Muscular Dystrophy

February 9, 2017 – The U.S. Food and Drug Administration today approved Emflaza (deflazacort) tablets and oral suspension to treat patients age 5 years and older with Duchenne muscular dystrophy...

FDA Approves Exondys 51 (eteplirsen) for Duchenne Muscular Dystrophy

September 19, 2016 – The U.S. Food and Drug Administration today approved Exondys 51 (eteplirsen) injection, the first drug approved to treat patients with Duchenne muscular dystrophy (DMD). Exondys...

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Duchenne Muscular Dystrophy, Spinal Muscular Atrophy