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Medically reviewed by Leigh Ann Anderson, PharmD. Last updated on July 15, 2025.
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Does Xenpozyme cure acid sphingomyelinase deficiency (ASMD)?
Medically reviewed by Carmen Pope, BPharm. Last updated on Nov 1, 2024.
Medically reviewed by Carmen Pope, BPharm. Last updated on Oct 31, 2024.
Medically reviewed by Carmen Pope, BPharm. Last updated on Oct 30, 2024.
Medically reviewed by Carmen Pope, BPharm. Last updated on July 21, 2025.
Medically reviewed by Carmen Pope, BPharm. Last updated on July 18, 2025.
Medically reviewed by Carmen Pope, BPharm. Last updated on Sep 1, 2023.
Medically reviewed by Philip Thornton, DipPharm. Last updated on Oct 30, 2024.
Medically reviewed by Leigh Ann Anderson, PharmD. Last updated on Oct 29, 2024.
Medically reviewed by Carmen Pope, BPharm. Last updated on Oct 8, 2024.