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Miplyffa News
FDA Approves Miplyffa for Treatment of Niemann-Pick Disease, Type C
MONDAY, Sept. 30, 2024 – The U.S. Food and Drug Administration has approved Miplyffa (arimoclomol), an oral medication for the treatment of Niemann-Pick disease, type C (NPC). Miplyffa, in...
FDA Approves Miplyffa (arimoclomol) for the Treatment of Niemann-Pick Disease Type C
CELEBRATION, Fla., Sept. 20, 2024 (GLOBE NEWSWIRE) – Zevra Therapeutics, Inc. (NasdaqGS: ZVRA) (Zevra, or the Company), a commercial-stage rare disease therapeutics company, today announced that the ...