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CLN2 Disease News
Related terms: Classic Late Infantile Neuronal Ceroid Lipofuscinosis, Neuronal Ceroid Lipofuscinosis Type 2, Late-Infantile Batten Disease
U.S. Food and Drug Administration Approves BioMarin's Brineura (cerliponase alfa) for Children Under 3 Years with CLN2 Disease
SAN RAFAEL, Calif., July 24, 2024 /PRNewswire/ – BioMarin Pharmaceutical Inc. (Nasdaq: BMRN) today announced that the U.S. Food and Drug Administration (FDA) has approved the company's supplemental...
FDA Approves Brineura (cerliponase alfa) for CLN2 Disease, a Form of Batten Disease
April 27, 2017 – The U.S. Food and Drug Administration today approved Brineura (cerliponase alfa) as a treatment for a specific form of Batten disease. Brineura is the first FDA-approved treatment...