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Acid Sphingomyelinase Deficiency Questions
Related terms: ASMD, Sphingolipidosis
Displaying 2 questions associated with Acid Sphingomyelinase Deficiency.
How does Xenpozyme work?
Does Xenpozyme cure acid sphingomyelinase deficiency (ASMD)?
How effective is Xenpozyme?
How quickly does Xenpozyme (olipudase alfa-rpcp) work?