Translarna FDA Approval Status
FDA Approved: No
Brand name: Translarna
Generic name: ataluren
Company: PTC Therapeutics, Inc.
Treatment for: Duchenne Muscular Dystrophy
Translarna (ataluren) is a protein restoration therapy in development for the treatment of nonsense mutation Duchenne muscular dystrophy (nmDMD).
Development timeline for Translarna
Further information
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