Naglazyme BioMarin Pharmaceutical Inc. - Treatment for Mucopolysaccharidosis VI (MPS VI)
Naglazyme (formerly rhASB) is an enzyme-replacement therapy for treatment of mucopolysaccharidosis VI (MPS VI), an inherited, life-threatening lysosomal storage disorder caused by a deficiency of the lysosomal enzyme N-acetylgalactosamine 4-sulfatase (also known as arylsulfatase B).Related Articles:
BioMarin Submits U.S. Biologics License Application for Marketing Authorization of Aryplase for MPS VI - November 29, 2004
FDA Drug Approvals Archive
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