Is there a specific age range for which Exondys 51 will work?
There is currently no specific age range specified for using Exondys 51, but a two-part Phase 3 study scheduled to run until 2026 has recruited boys and young men aged 4 though 21 who meet the study criteria. Previous studies have only investigated boys up to age 19 years. Symptoms of Duchenne muscular dystrophy (DMD) usually appear between 3 and 5 years of age and the condition primarily affects boys at a rate of about 1 in every 3,600 male infants born. If you have an older child, the best thing you can do is talk to your doctor about Exondys 51 treatment.
References
- Madesen A. Top 5 FAQs: Eteplirsen (Exondys 51) for DMD Treatment Sept 2016. MDA News. https://strongly.mda.org/eteplirsen-exondys-51-dmd-treatment-top-5-frequently-asked-questions/
- Exondys 51. Sarepta https://www.exondys51.com/faqs
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