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Acid Sphingomyelinase Deficiency Support Group

Related terms: ASMD, Sphingolipidosis

Summary

Our support group for Acid Sphingomyelinase Deficiency has 2 questions and 3 members. Updated 22 Nov 2022.

Latest questions

How effective is Xenpozyme?

How does Xenpozyme work?

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Latest news

FDA Approves Xenpozyme (olipudase alfa-rpcp) for Non-CNS Manifestations of Acid Sphingomyelinase Deficiency (ASMD)

Paris, August 31, 2022 – The U.S. Food and Drug Administration (FDA) has approved Xenpozyme (olipudase alfa-rpcp)…

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