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Vyndamax
Vyndamax may be given to reduce death or hospitalization caused by heart problems in adults with ...
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Tegsedi
Tegsedi (inotersen) is an RNA-targeting treatment that may be used to reduce the symptoms of ...
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Vyndaqel
Vyndaqel (tafamidis meglumine) is a transthyretin stabilizer that may be given to reduce death or ...
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Wainua
Wainua (eplontersen) is used to treat polyneuropathy of hereditary transthyretin-mediated ...
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Amvuttra
Amvuttra is used to treat polyneuropathy associated with hereditary transthyretin-mediated ...
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Zolgensma
Zolgensma (onasemnogene abeparvovec-xioi) is gene therapy used for spinal muscular atrophy. It is a ...
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Evrysdi
Evrysdi is used to treat spinal muscular atrophy (SMA) in adults, children, and infants. It is ...
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