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Gene Therapy Shows Promise for Inherited Eye Disease

Posted 4 May 2015 by Drugs.com

SUNDAY, May 3, 2015 – A new study finds that gene therapy quickly improves eyesight for patients who've lost their vision from an inherited condition called Leber congenital amaurosis (LCA). But the improvements aren't permanent: Researchers said the gains began to diminish after one to three years. "Gene therapy for LCA demonstrated we could improve vision in previously untreatable and incurable retinal conditions," study leader Dr. Samuel Jacobson, of the University of Pennsylvania's Scheie Eye Institute, said in a U.S. National Eye Institute release. "Even though the current version of the therapy doesn't appear to be the permanent treatment we were hoping for, the gain in knowledge ... is an opportunity to improve the therapy so that the restored vision can be sustained for longer durations in patients," Jacobson added. Scientists started the research in 2007, looking at 15 people ... Read more

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