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Hemophilia News

Another Gene Therapy Breakthrough Against Hemophilia

Posted 10 Dec 2017 by Drugs.com

SATURDAY, Dec. 9, 2017 – Coming just days after reports of a gene therapy that pushed the bleeding disorder hemophilia B into remission, new research suggests the same could be true for adults with the "A" form of the disease. That's significant because, due to the complexities of the gene responsible for hemophilia A, experts had thought it might be far more resistant to gene-based treatment. ...

Gene Therapy May Allow Hemophilia Patients to Go Without Meds

Posted 7 Dec 2017 by Drugs.com

WEDNESDAY, Dec. 6, 2017 – Gene therapy has helped 10 men with a form of the bleeding disorder hemophilia produce a critical blood clotting factor. This could eliminate the need for tedious and costly standard treatments, researchers report. While saying the one-time gene therapy was an ideal treatment goal because of its effects, the researchers stopped short of calling it a cure for hemophilia ...

FDA Approves Hemlibra (emicizumab-kxwh) for Hemophilia A with Inhibitors

Posted 20 Nov 2017 by Drugs.com

November 16, 2017 – The U.S. Food and Drug Administration today approved Hemlibra (emicizumab-kxwh) to prevent or reduce the frequency of bleeding episodes in adult and pediatric patients with hemophilia A who have developed antibodies called Factor VIII (FVIII) inhibitors. “Reducing the frequency or preventing bleeding episodes is an important part of disease management for patients with h ...

Is Blood Donated by Mothers Less Safe for Men?

Posted 17 Oct 2017 by Drugs.com

TUESDAY, Oct. 17, 2017 – Men who receive blood donated by previously pregnant women may face an increased risk of death following the transfusion, a new study from the Netherlands suggests. Males transfused with blood from a woman with a history of pregnancy appear to be 13 percent overall more likely to die in coming years, compared with those who received blood from another man, said ...

First Test to Detect Zika in Blood Donations Approved

Posted 7 Oct 2017 by Drugs.com

FRIDAY, Oct. 6, 2017 – The cobas Zika test has been approved by the U.S. Food and Drug Administration – the first approved screening test to detect the Zika virus in blood donations. The test is not designed to diagnose any particular person's Zika infection, however, the FDA said. In August 2016, the agency recommended that all U.S. states and territories screen blood for Zika, according to an ...

Health Tip: Giving Blood

Posted 4 Oct 2017 by Drugs.com

-- Donating blood for the first time may sound intimidating. But the process is fairly painless, takes only about 20 minutes and could help save a life. The American Red Cross explains the different types of blood donation: Whole blood – The most common and quickest type of donation, involving a pint of whole blood. The donation is typically separated into transfusable components, including red ...

FDA Approves Rebinyn (Coagulation Factor IX (Recombinant), GlycoPEGylated) for Patients with Hemophilia B

Posted 27 Jun 2017 by Drugs.com

PLAINSBORO, N.J., May 31, 2017 /PRNewswire/ – Novo Nordisk today announced that the U.S. Food and Drug Administration (FDA) has approved the Biologics License Application for Rebinyn (Coagulation Factor IX (Recombinant), GlycoPEGylated) for the treatment of adults and children with hemophilia B. Hemophilia B is a chronic and inherited bleeding disorder that affects approximately 5,000 people in ...

FDA OKs 1st At-Home Genetic Tests for 10 Disorders

Posted 6 Apr 2017 by Drugs.com

THURSDAY, April 6, 2017 – The U.S. Food and Drug Administration has approved the first home genetic tests for 10 health risks, including Parkinson's disease and late-onset Alzheimer's. The approval – granted to the California-based company 23andMe Inc. – could help test users make lifestyle choices or spark important discussions with health care providers, the FDA said. "Consumers can now have ...

Gene Therapy Offers Hope to Some Hemophilia Patients

Posted 6 Dec 2016 by Drugs.com

TUESDAY, Dec. 6, 2016 – Preliminary research suggests that a single dose of an experimental gene therapy may help patients with hemophilia B. As explained by the National Hemophilia Foundation, hemophilia B is a genetic disorder where people lack a protein needed for blood clotting called factor IX, or that the type of factor IX they produce is defective. The condition can lead to excess ...

Two New Findings Offer Hope for Those With Severe Hemophilia

Posted 26 May 2016 by Drugs.com

WEDNESDAY, May 25, 2016 – Two new studies could pave the way to major changes in how doctors treat severe cases of hemophilia – a rare genetic disorder that can cause uncontrolled bleeding. Both studies tackle a key challenge: Up to one-third of children with severe hemophilia develop antibodies against the standard therapy. But one study highlights the value of an old therapy, while the other ...

Review Finds Mixed Success With Hemophilia Treatment

Posted 16 Mar 2016 by Drugs.com

WEDNESDAY, March 16, 2016 – Though the past 50 years have brought major treatment advances, men with severe hemophilia are still at high risk for bleeding and physical disability, experts say. Hemophilia is a genetic disease that prevents blood from clotting normally, leading to an increased risk of serious bleeding. More common in men than in women, it affects about one out of every 5,000 men, ...

FDA Approves Nuwiq (Antihemophilic Factor [Recombinant]) for Hemophilia A

Posted 17 Sep 2015 by Drugs.com

HOBOKEN, N.J. September 15th, 2015: Octapharma USA today announced the U.S. Food and Drug Administration (FDA) has approved Nuwiq, Antihemophilic Factor (Recombinant), an intravenous therapy for adults and children living with Hemophilia A. The Nuwiq approval includes on-demand treatment and control of bleeding episodes; routine prophylaxis to reduce the frequency of bleeding episodes; and ...

Kids' Hemophilia Drugs a Big Part of State Medicaid Spending

Posted 31 Jul 2015 by Drugs.com

FRIDAY, July 31, 2015 – Treatment costs for one childhood illness, hemophilia, may use up a big chunk of a state's Medicaid budget, a new study out of California shows. The researchers found that treatments for hemophilia – a rare, inherited disorder in which blood does not clot normally – accounted for the largest share of spending on outpatient drugs among publicly insured children in ...

FDA Approves Obizur [Antihemophilic Factor (Recombinant)] for Acquired Hemophilia A

Posted 27 Oct 2014 by Drugs.com

DEERFIELD, Ill., October 24, 2014 - Baxter International Inc. today announced that the United States Food and Drug Administration (FDA) has approved Obizur [Antihemophilic Factor (Recombinant), Porcine Sequence] for the treatment of bleeding episodes in adults with acquired hemophilia A (AHA), a very rare and potentially life-threatening acute bleeding disorder. Obizur was granted orphan-drug ...

New Treatment Obizur Approved for Rare Form of Hemophilia

Posted 24 Oct 2014 by Drugs.com

FRIDAY, Oct. 24, 2014 – Obizur (antihemophilic factor recombinant) has been approved to treat a rare, non-inherited form of hemophilia in adults. Unlike the more common form of hemophilia that's inherited and affects males, acquired hemophilia affects both males and females. The rarer form of the blood disorder occurs when the body's immune system attacks a protein that's necessary for normal ...

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Hemophilia A, Hemophilia B, Coagulation Defects and Disorders